14:20-14:35 Diamond-Blackfan anaemia Lydie Da Costa (Paris)
14:35-14:50 Germline predisposition to MDS and bone marrow failure Akiko Shimamura (Boston)
14:50-14:57 Haploidentical Stem Cell Transplantation for High Risk
Haemoglobinopathies Using Post-Transplant Cyclophosphamide Du’A Darabseh (Amman)
14:57-15:30 Panel discussion
SESSION VIII – Gene Therapy/Editing
Chairs: John Porter (London), Maria-Domenica Cappellini (Milan)
15:30-15:35 Introduction John Porter (London)
Maria-Domenica Cappelini (Milan)
15:35-15:50 Who is the best patient candidate for gene therapy? Vip Viprakasit (Bangkok)
15:50-16:05 Gene therapy in haemoglobinopathies vs BMT Marina Cavazzana (Paris)
16:05-16:20 Gene therapy in haemoglobinopathies vs gene editing Mitchell Weiss (Memphis)
16:20-16:35 Focus on : Immunotherapy and CAR-T in MDS:
Dream or reality? Rafael Bejar (La Jolla)
16:35-17:05 Panel discussion
17:05-17:15 Break
SESSION IX – Drugs and ineffective erythropoiesis
Chairs: Ali Taher (Beirut), Antonio Piga (Turin)
17:15-17:20 Introduction Ali Taher (Beirut)
Antonio Piga (Turin)
17:20-17:35 Iron restricted erythropoiesis Tomas Ganz (Los Angeles)
17:35-17:50 New approaches to anaemia of MDS Uwe Platzbecker (Leipzig)
17:50-18:05 New approaches to the management of sickle cell disease Lucia De Franceschi (Verona)
18:05-18:12 Inclusion of a shRNA Targeting BCL11A into
a β-Globin Expressing Vector Allows Concurrent
Synthesis of Curative Adult and Fetal Hemoglobin Danuta Jarocha (Philadelphia)
18:12-18:42 Panel discussion
18:42-19:00 Closing remarks
4
SCIENTIFIC PROGRAMME
SESSION I
BONE MARROW
RESPONSE TO VIRAL
INFECTIONS
SESSION II
HAEMATOLOGICAL
RESPONSE TO SARS
COV2 INFECTION
SESSION III
DYSERYTHROPOIESIS IN
CLONAL HAEMOPOIESIS
AND MDS
SESSION IV
ERYTHROPOIESIS
CONTROL
SESSION V
ERYTHROPOIESIS
CONTROL : PHASE 2
SESSION VI
IRON METABOLISM
AND ERYTHROPOIESIS
SESSION VII
INHERITED
DYSERYTHROPOIESIS
SESSION VIII
GENE THERAPY/EDITION
SESSION IX – DRUGS
AND INEFFECTIVE
ERYTHROPOIESIS
SELECTED ABSTRACTS
FOR AN ORAL
PRESENTATION
SELECTED ABSTRACTS
FOR A POSTER
PRESENTATION
FACULTY DISCLOSURES